BrAAVe | Clinical Research Studies Listing

Recruiting

99 years or below

All

Phase N/A

5 participants needed

1 Location

Brief description of study

This is a study evaluating SAR446268 as a treatment for DM1. SAR446268 is designed to deliver miRNA to pathological DMPK gene expression that leads to DM1. Patients will receive a 1-time dose of the study drug and then undergo a 5 year follow-up period to monitor safety and efficacy.

Eligibility of study

You may be eligible for this study if you meet the following criteria:

Conditions: Medical Research
Age: 99 years or below
Gender: All

TBD

Updated on 17 Jun 2026. Study ID: 26-6047

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