Fortify - MLB-01-005

Recruiting

99 years and younger

All

Phase N/A

1 Location

Brief description of study

Limb-Girdle Muscular Dystrophy Type 2I (LGMD2I) is also known as LGMD R9 FKRP-related and is therefore referred to as LGMD2I/R9 . This study will evaluate the safety and efficacy of long-term administration of BBP-418 in patients with LGMD2I/R9. The study will include patients ages 12 to 60, consistent with the existing preclinical toxicology profile. This will encompass the significant majority of existing diagnosed patients based upon the established epidemiology of the disease.

Eligibility of study

You may be eligible for this study if you meet the following criteria:

Conditions:
Medical Research
Age: - 99 Years
Gender: All

TBD

Updated on 13 Mar 2024. Study ID: 853368

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