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Found 4 Hemophilia trials

A listing of Hemophilia medical research trials actively recruiting patient volunteers. Search for closest city to find more detailed information on a research study in your area.

 Phase 3  open label  single arm study to evaluate efficacy and safety of FIX gene transfer with PF-06838435 (rAAV Spark100-hFIX-Padua) in adult male participants with moderately severe to severe hemophilia B (FIX:C= or -2%) (BeneGene-2)
99 years or below
All genders
Phase 3
The research study is being conducted to test the safety and effectiveness of the study drug which is a gene therapy based treatment. Researchers want to see if the drug works to prevent the bleeding episodes commonly experienced by patient with Hemophilia B and to advance science and medicine. Subjects …
99 years or below
All genders
To evaluate the efficacy of SPK-8011 in preventing bleed episodes compared with FVIII prophylaxis in patients with hemophilia A without FVIII inhibitors on routine FVIII prophylaxis. To evaluate the efficacy of SPK-8011 in preventing bleed episodes compared with FVIII prophylaxis in patients with hemophilia A without FVIII inhibitors on routine …
99 years or below
All genders
Primary- testing of the safety and tolerability at increasing doses of SR604 given every 4 weeks subcutaneously in subjects with hemophilia A or B with or without inhibitors. Secondary- testing the pharmacokinetics (PK) and clinical activity of SR604 Exploratory- testing the immunogenicity, pharmacodynamics by way of SR604 activity, inflammatory responses, …
99 years or below
All genders
The primary objective of the present study is to evaluate the efficacy (effectiveness) of prophylactic (preventative doses) of emicizumab (FDA approved, also called Hemlibra) administered on a regular scheduled basis to prevent bleeds in patients with acquired hemophilia A (AHA). The secondary objectives are to study the safety of emicizumab …