A listing of Hemophilia medical research trials actively recruiting patient volunteers. Search for closest city to find more detailed information on a research study in your area.
The research study is being conducted to test the safety and effectiveness of the study drug which is a gene therapy based treatment. Researchers want to see if the drug works to prevent the bleeding episodes commonly experienced by patient with Hemophilia B and to advance science and medicine. Subjects …
To evaluate the efficacy of SPK-8011 in preventing bleed episodes compared with FVIII prophylaxis in patients with hemophilia A without FVIII inhibitors on routine FVIII prophylaxis. To evaluate the efficacy of SPK-8011 in preventing bleed episodes compared with FVIII prophylaxis in patients with hemophilia A without FVIII inhibitors on routine …
Primary- testing of the safety and tolerability at increasing doses of SR604 given every 4 weeks subcutaneously in subjects with hemophilia A or B with or without inhibitors. Secondary- testing the pharmacokinetics (PK) and clinical activity of SR604 Exploratory- testing the immunogenicity, pharmacodynamics by way of SR604 activity, inflammatory responses, …
The primary objective of the present study is to evaluate the efficacy (effectiveness) of prophylactic (preventative doses) of emicizumab (FDA approved, also called Hemlibra) administered on a regular scheduled basis to prevent bleeds in patients with acquired hemophilia A (AHA). The secondary objectives are to study the safety of emicizumab …