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Found 4 adreeja-guharay trials

A listing of adreeja-guharay medical research trials actively recruiting patient volunteers. Search for closest city to find more detailed information on a research study in your area.

 A  STUDY TO ASSESS THE LONG-TERM SAFETY AND EFFICACY OF INTRAVENOUS ATB200 CO-ADMINISTERED WITH ORAL AT2221 IN ADULT SUBJECTS WITH LATE-ONSET POMPE DISEASE

A STUDY TO ASSESS THE LONG-TERM SAFETY AND EFFICACY OF INTRAVENOUS ATB200 CO-ADMINISTERED WITH ORAL AT2221 IN ADULT SUBJECTS WITH LATE-ONSET POMPE DISEASE

18-99 years
All genders
Phase 3
Interventional
A STUDY TO ASSESS THE LONG-TERM SAFETY AND EFFICACY OF INTRAVENOUS ATB200 CO-ADMINISTERED WITH ORAL AT2221 IN ADULT SUBJECTS WITH LATE-ONSET POMPE DISEASE

Platform Trial

99 years and younger
All genders
The phase 2/3 HEALEY ALS Platform Trial is a perpetual multi-center, multi-regimen clinical trial evaluating the safety and efficacy of investigational products (IP) for the treatment of ALS. IPs are tested in trial regimens (Regimen-Specific Appendix (RSA)). Patients will be randomized twice, first to one of the regimens, and second …

EDG-5506-201

99 years and younger
All genders
This is a multicenter, randomized, Phase 2, double-blind, placebo-controlled study to evaluate the effect of EDG-5506 on the safety, PK, biomarkers, and functional measures in adult and adolescent participants with BMD. This randomized, double-blind, placebo-controlled study will evaluate the safety, pharmacokinetics (PK), and efficacy of EDG-5506 in adults and adolescents …

Fortify - MLB-01-005

99 years and younger
All genders
Limb-Girdle Muscular Dystrophy Type 2I (LGMD2I) is also known as LGMD R9 FKRP-related and is therefore referred to as LGMD2I/R9 . This study will evaluate the safety and efficacy of long-term administration of BBP-418 in patients with LGMD2I/R9. The study will include patients ages 12 to 60, consistent with the …